Global Thalassemia Industry Report ? Global Market Scenario and Growth strategie

Posted by daniel1244martinez on August 27th, 2017

Global Markets Direct’s latest Pharmaceutical and Healthcare disease pipeline guide Thalassemia – Pipeline Review, H2 2017, provides an overview of the Thalassemia (Hematological Disorders) pipeline landscape.

Thalassemia is a group of inherited blood disorders that affect the body’s ability to produce hemoglobin and red blood cells. Symptoms include fussiness, paleness, frequent infections, failure to thrive, poor appetite and jaundice. Predisposing factors include family history. Treatment includes blood transfusions and bone marrow transplant.

Browse Full Table of Contents and Report Description @ https://www.reportsmonitor.com/thalassemia-pipeline-review-h2-2017/

Report Highlights

Global Markets Direct’s Pharmaceutical and Healthcare latest pipeline guide Thalassemia – Pipeline Review, H2 2017, provides comprehensive information on the therapeutics under development for Thalassemia (Hematological Disorders), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.

The Thalassemia (Hematological Disorders) pipeline guide also reviews of key players involved in therapeutic development for Thalassemia and features dormant and discontinued projects. The guide covers therapeutics under Development by Companies /Universities /Institutes, the molecules developed by Companies in Phase III, Phase II, Phase I, Preclinical and Discovery stages are 2, 5, 8, 15 and 2 respectively. Similarly, the Universities portfolio in Phase II, Preclinical and Discovery stages comprises 2, 2 and 1 molecules, respectively.

Thalassemia (Hematological Disorders) pipeline guide helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage. The guide is built using data and information sourced from Global Markets Direct’s proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.

Note: Certain content / sections in the pipeline guide may be removed or altered based on the availability and relevance of data.

Scope

– The pipeline guide provides a snapshot of the global therapeutic landscape of Thalassemia (Hematological Disorders).

– The pipeline guide reviews pipeline therapeutics for Thalassemia (Hematological Disorders) by companies and universities/research institutes based on information derived from company and industry-specific sources.

– The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages.

– The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities.

– The pipeline guide reviews key companies involved in Thalassemia (Hematological Disorders) therapeutics and enlists all their major and minor projects.

– The pipeline guide evaluates Thalassemia (Hematological Disorders) therapeutics based on mechanism of action (MoA), drug target, route of administration (RoA) and molecule type.

– The pipeline guide encapsulates all the dormant and discontinued pipeline projects.

– The pipeline guide reviews latest news related to pipeline therapeutics for Thalassemia (Hematological Disorders)

Reasons to buy

– Procure strategically important competitor information, analysis, and insights to formulate effective R&D strategies.

– Recognize emerging players with potentially strong product portfolio and create effective counter-strategies to gain competitive advantage.

– Find and recognize significant and varied types of therapeutics under development for Thalassemia (Hematological Disorders).

– Classify potential new clients or partners in the target demographic.

– Develop tactical initiatives by understanding the focus areas of leading companies.

– Plan mergers and acquisitions meritoriously by identifying key players and it’s most promising pipeline therapeutics.

– Formulate corrective measures for pipeline projects by understanding Thalassemia (Hematological Disorders) pipeline depth and focus of Indication therapeutics.

– Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope.

– Adjust the therapeutic portfolio by recognizing discontinued projects and understand from the know-how what drove them from pipeline.

For Requesting a Sample Copy of This Report, Please Visit @ https://goo.gl/F55qZp

Table of Content

Table of Contents 2

List of Tables 4

List of Figures 4

Introduction 5

Global Markets Direct Report Coverage 5

Thalassemia – Overview 6

Thalassemia – Therapeutics Development 7

Pipeline Overview 7

Pipeline by Companies 8

Pipeline by Universities/Institutes 11

Products under Development by Companies 12

Products under Development by Universities/Institutes 14

Thalassemia – Therapeutics Assessment 15

Assessment by Target 15

Assessment by Mechanism of Action 17

Assessment by Route of Administration 19

Assessment by Molecule Type 21

Thalassemia – Companies Involved in Therapeutics Development 23

Acceleron Pharma Inc 23

Agios Pharmaceuticals Inc 23

Alnylam Pharmaceuticals Inc 24

bluebird bio Inc 24

Cadila Healthcare Ltd 25

Calimmune Inc 25

CRISPR Therapeutics 26

Editas Medicine Inc 26

Errant Gene Therapeutics LLC 27

Gamida Cell Ltd 27

Gilead Sciences Inc 28

Incyte Corp 28

Ionis Pharmaceuticals Inc 29

IRBM Science Park SpA 29

Kiadis Pharma NV 30

La Jolla Pharmaceutical Company 30

Merck & Co Inc 31

Protagonist Therapeutics Inc 31

Sangamo Therapeutics Inc 32

Thalassemia – Drug Profiles 33

(decitabine + tetrahydrouridine) – Drug Profile 33

ACY-957 – Drug Profile 34

AG-348 – Drug Profile 37

ALN-TMP – Drug Profile 42

ambrisentan – Drug Profile 44

ATIR-201 – Drug Profile 47

BB-305 – Drug Profile 48

benserazide – Drug Profile 57

CAL-H – Drug Profile 59

CordIn – Drug Profile 60

Drugs to Chelate Iron for Bone Degeneration, Postmenopausal Osteoporosis and Thalassemia – Drug Profile 61

Gene Therapy for Sickle Cell Disease and Thalassemia – Drug Profile 62

Gene Therapy to Activate IGF2BP1 for Sickle Cell Disease and Thalassemia – Drug Profile 63

GSK-2696277 – Drug Profile 64

IMR-687 – Drug Profile 65

IONISTMPRSS-6LRx – Drug Profile 66

LJPC-401 – Drug Profile 67

luspatercept – Drug Profile 69

M-009 – Drug Profile 78

M-012 – Drug Profile 79

NiCord – Drug Profile 81

PEG-EPO – Drug Profile 85

PHBB-101 – Drug Profile 86

PTG-300 – Drug Profile 87

RCY-1497 – Drug Profile 88

RNAi Gene Therapy for Sickle Cell Disease and Beta Thalassemia – Drug Profile 89

ruxolitinib phosphate – Drug Profile 90

SCD-101 – Drug Profile 105

sirolimus – Drug Profile 106

Small Molecule to Inhibit Histone Deacetylase 1 for Beta Thalassemia – Drug Profile 107

Small Molecules to Inhibit PRMT5 for Haemoglobinopathies and Solid Tumours – Drug Profile 108

sotatercept – Drug Profile 109

ST-400 – Drug Profile 114

Stem Cell Therapy for Beta Thalassemia and Sickle Cell Disease – Drug Profile 116

Stem Cell Therapy for Beta Thalassemia and Sickle Cell Disease – Drug Profile 117

Stem Cell Therapy to Activate Hemoglobin Beta for Beta-Thalassemia – Drug Profile 119

Thalagen – Drug Profile 120

Thalassemia – Dormant Projects 121

Thalassemia – Product Development Milestones 122

Featured News & Press Releases 122

Appendix 137

Methodology 137

Coverage 137

Secondary Research 137

Primary Research 137

Expert Panel Validation 137

Contact Us 137

Disclaimer 138

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daniel1244martinez
Joined: August 4th, 2017
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